GMG patients were more likely to receive both GC and tacrolimus earlier than the corresponding OMG cases. Patients with juvenile myasthenia gravis (JMG) who received treatment with tacrolimus within a ...

This newly developed PROM assessing mental health in hemophilia can be used to track progress throughout treatment. Researchers developed a novel mental health patient-reported outcome measure (PROM) ...

Researchers from the United States presented the case of a patient with myelofibrosis (MF) being treated with ruxolitinib who had cavitary lung lesions caused by a Pneumocystis jirovecii infection.

The mean annual rate of forced vital capacity percent decline improved from - 3.2% before surgery to -6.9% after surgery in patients with SMA type 2. Scoliosis surgery seems to have a positive impact ...

Benjamin Lou, a student at the Massachusetts Institute of Technology who has spinal muscular atrophy, works on his laptop (Photo by Larry Luxner) Benjamin Lou, 21, leads a team of engineers who are ...

The management of advanced hemophilic joint arthropathy requires multidisciplinary input and coordination. In Healthcare, physicians presented the long surgical history of a patient with severe ...

In short, these results revealed that both CRLF2 OE and CRLF2-d are correlated with poor prognosis in ALL patients. Cytokine receptor-like factor 2 (CRLF2) overexpression appears to correlate with ...

Durvalumab-induced MG appears to be rare, with some studies, such as the randomized PACIFIC trial, reporting an incidence below 1%. A comprehensive review regarding the incidence, mechanisms, and ...

The landscape of ATTR-CM has experienced major advancements due, in part, to increased disease awareness and use of specific treatments targeted at the disorder. Among patients with ...

I recently read a post from someone with cold agglutinin disease (CAD) that details how she was recently diagnosed and how awful it has been for her. We can all relate, as there are moments when CAD ...

Sebetralstat is poised to become the first oral, on-demand treatment for HAE, pending FDA approval. The US Food and Drug Administration (FDA) has accepted KalVista Pharmaceuticals’ New Drug ...

The sole clinical symptom of the patient was polyurea. The infiltration of leukemic blasts into the kidney can lead to nephrogenic diabetes insipidus in patients with acute lymphoblastic leukemia (ALL ...